Centogene has expanded its partnership with PTC Therapeutics to make its genetic and biomarker testing services —…
Articles by Joana Carvalho, PhD
Scientists discovered four potential protein biomarkers — apolipoprotein D, apolipoprotein H, oligodendrocyte myelin glycoprotein, and collagen6A3…
Gene therapy with small RNA molecules may be a promising therapeutic strategy to correct RNA processing errors in aromatic l-amino…
Since its founding in 2013, the International Working Group on Neurotransmitter related Disorders (iNTD) has been building a network…
Gene therapy using a special type of virus vector to deliver the functional DDC gene is well-tolerated and might improve…
Only 18 months after its initial licensing, Agilis Biotherapeutics‘ gene therapy for aromatic l-amino acid decarboxylase (AADC) deficiency has been deemed ready…