Recent Posts
- NORD: Rare Disease Advocates in ‘Unique Position’ to Educate Congress
- Honoring the Passionate Teachers Who Make a Difference
- Curant Health Designated a Partner in Rare Disease Advocacy
- Improving Caregiver Collaboration Through Virtual Meetups
- Centogene, Premier Research Team Up to Boost Trial Enrollments
- Life Comes Full Circle as I Reflect on Our Journey With AADC Deficiency
- Medable, Every Cure Partner on Drug Repurposing for Rare Diseases
- Our Family Returns to Taiwan to Join a 2nd AADC Deficiency Study
- Coalition Calls for New Commitment as FDA Orphan Drug Act Turns 40
- Connecting With Professionals to Improve Patient Experiences