The ongoing clinical evaluation of a new gene therapy to treat aromatic L-amino acid decarboxylase (AADC) deficiency has been…
Articles by Steve Bryson, PhD
The investigational gene therapy PTC-AADC safely led to profound improvements in children with aromatic L-Amino acid decarboxylase (AADC)…
Using PTC-AADC gene therapy in children with aromatic l-amino acid decarboxylase (AADC) deficiency was found to be relatively…
An Italian panel of experts recommends using vitamin B6, dopamine agonists, and monoamine oxidase inhibitors (MAOIs) as first-line…
Systematic analysis of non-invasive MRI brain scans of people with aromatic l-amino acid decarboxylase…
The development of new gene therapy to treat people with aromatic L-amino acid decarboxylase (AADC)…
A simple urine test using widely available methods may help diagnose people with aromatic L-amino…